STRC Research
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Tag: pediatric
2 items with this tag.
Apr 14, 2026
Gene Therapy for Infants and Children With Otoferlin-Related Auditory Neuropathy Spectrum Disorder
gene-therapy
hearing-loss
otoferlin
otof
auditory-neuropathy
clinical-trial
pediatric
fda-pathway
Mar 18, 2026
Mendell_2020_micro_dystrophin_clinical
AAV
clinical-trial
micro-dystrophin
Duchenne
Phase1-2
rAAVrh74
gene-therapy
pediatric