STRC Research

Tag: micro-dystrophin

1 item with this tag.

  • Mar 18, 2026

    Mendell_2020_micro_dystrophin_clinical

    • AAV
    • clinical-trial
    • micro-dystrophin
    • Duchenne
    • Phase1-2
    • rAAVrh74
    • gene-therapy
    • pediatric

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