Dual Vector AAV Strategy

A gene therapy delivery approach where the therapeutic gene is split across two AAV vectors that recombine inside target cells. Required for large genes that exceed single AAV packaging capacity (~4.7 kb).

Relevance to Misha: STRC gene (~6 kb coding) exceeds single AAV capacity. Iranfar et al. (2026) demonstrated dual-vector AAV delivery of STRC with functional restoration in mouse models.

Connections